Genetics: Gene Therapy

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Topic / Topic starter Repliessort descending Last post
Normal topic One Morpholino oligo dose rescues spinal muscular atrophy in mouse
by Jon Moulton » Wed, 12/21/2011 - 12:43
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by Jon Moulton
Wed, 12/21/2011 - 12:43
Normal topic Exon skipping for SMN2: Toward a Treatment for SMA
by Jon Moulton » Fri, 04/26/2013 - 08:37
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by Jon Moulton
Fri, 04/26/2013 - 08:37
Normal topic Challenges to oligonucleotides-based therapeutics for Duchenne MD
by Jon Moulton » Fri, 02/11/2011 - 12:34
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by Jon Moulton
Fri, 02/11/2011 - 12:34
Normal topic Long-term 10-oligo cocktail in mice for muscular dystrophy
by Jon Moulton » Wed, 02/04/2015 - 16:41
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by Jon Moulton
Wed, 02/04/2015 - 16:41
Normal topic RNA approaches for treatment of SMA in human motor neurons
by Jon Moulton » Wed, 07/01/2015 - 18:22
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by Jon Moulton
Wed, 07/01/2015 - 18:22
Normal topic RNA therapeutics: beyond RNA interference and antisense oligonucleotides
by Jon Moulton » Tue, 01/24/2012 - 07:51
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by Jon Moulton
Tue, 01/24/2012 - 07:51
Normal topic genetic engineering and xenotransplantation
by hilltrekker » Thu, 03/19/2009 - 11:37
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by hilltrekker
Thu, 03/19/2009 - 11:37
Normal topic Make or break for first splice-modulating agents
by Jon Moulton » Mon, 11/04/2013 - 20:41
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by Jon Moulton
Mon, 11/04/2013 - 20:41
Normal topic RNA Splicing Manipulation: therapeutics review
by Jon Moulton » Thu, 04/07/2011 - 14:37
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by Jon Moulton
Thu, 04/07/2011 - 14:37
Normal topic Systemically Skipping Human Dystrophin Exons in Transgenic Mouse Model
by Jon Moulton » Thu, 05/19/2011 - 12:04
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by Jon Moulton
Thu, 05/19/2011 - 12:04
Normal topic Bodywide skipping of exons 45–55 mice: systemic antisense delivery
by Jon Moulton » Mon, 08/06/2012 - 15:24
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by Jon Moulton
Mon, 08/06/2012 - 15:24
Normal topic Parent advocacy of molecular medicine for Duchenne muscular dystrophy
by Jon Moulton » Thu, 03/06/2014 - 17:20
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by Jon Moulton
Thu, 03/06/2014 - 17:20
Normal topic Cardiac integrity& lasting systemic use of bare morpholinos for DMD
by Jon Moulton » Mon, 08/22/2011 - 14:51
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by Jon Moulton
Mon, 08/22/2011 - 14:51
Normal topic Exon-skipping drug pulls ahead in muscular dystrophy field
by Jon Moulton » Fri, 09/07/2012 - 12:12
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by Jon Moulton
Fri, 09/07/2012 - 12:12
Normal topic The Status of Exon Skipping as a Therapeutic Approach to Duchenne Muscular
by Jon Moulton » Thu, 10/28/2010 - 13:58
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by Jon Moulton
Thu, 10/28/2010 - 13:58
Normal topic Dystrophin repair, mdx mice: new muscle-homing peptide-morpholino conjugate
by Jon Moulton » Wed, 04/16/2014 - 15:52
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by Jon Moulton
Wed, 04/16/2014 - 15:52
Normal topic Splice-correction of mutations causing ataxia-telangiectasia
by Jon Moulton » Tue, 10/18/2011 - 12:14
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by Jon Moulton
Tue, 10/18/2011 - 12:14
Normal topic Dantrolene Enhances Antisense Exon Skipping in Human & Mouse Models of DMD
by Jon Moulton » Wed, 12/12/2012 - 14:27
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by Jon Moulton
Wed, 12/12/2012 - 14:27
Normal topic Chronic Low-dose PMO Ameliorate mdx Mouse Pathology, Walking Behavior
by Jon Moulton » Mon, 11/29/2010 - 12:16
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by Jon Moulton
Mon, 11/29/2010 - 12:16
Normal topic Morpholinos suppress mutant huntingtin expression & attenuate neurotoxicity
by Jon Moulton » Mon, 07/07/2014 - 18:23
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by Jon Moulton
Mon, 07/07/2014 - 18:23
Normal topic Restoring Dystrophin-associated Glycoprotein Complex by DMD Exon Skipping
by Jon Moulton » Fri, 11/18/2011 - 14:17
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by Jon Moulton
Fri, 11/18/2011 - 14:17
Normal topic Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe SMA mice
by Jon Moulton » Thu, 01/24/2013 - 11:44
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by Jon Moulton
Thu, 01/24/2013 - 11:44
Normal topic Evaluation of Exon-Skipping Strategies for Duchenne Muscular Dystrophy Util
by Jon Moulton » Mon, 01/24/2011 - 11:46
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by Jon Moulton
Mon, 01/24/2011 - 11:46
Normal topic Pompe Disease: Block making Glycogen Synthase 1 for Substrate Reduction
by Jon Moulton » Wed, 10/29/2014 - 15:50
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by Jon Moulton
Wed, 10/29/2014 - 15:50
Normal topic Muscular dystrophy podcasts
by Jon Moulton » Thu, 01/12/2012 - 12:33
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by Jon Moulton
Thu, 01/12/2012 - 12:33

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