Genetics: Gene Therapy

Pages

Topic / Topic starter Replies Last postsort ascending
Normal topic Marine-Based Therapies for Cancer
by atcg » Wed, 01/03/2007 - 01:42
0
by Jamie_Cruikshank
Mon, 03/07/2016 - 12:23
Normal topic RNA approaches for treatment of SMA in human motor neurons
by Jon Moulton » Wed, 07/01/2015 - 18:22
0
by Jon Moulton
Wed, 07/01/2015 - 18:22
Normal topic Eteplirsen, Morpholino to Treat DMD; 168 Week Data: 6MWT, PFT, and Safety
by Jon Moulton » Tue, 04/28/2015 - 21:00
0
by Jon Moulton
Tue, 04/28/2015 - 21:00
Normal topic Exon skipping approach to duchenne muscular dystrophy
by Jon Moulton » Fri, 02/13/2015 - 21:08
0
by Jon Moulton
Fri, 02/13/2015 - 21:08
Normal topic Long-term 10-oligo cocktail in mice for muscular dystrophy
by Jon Moulton » Wed, 02/04/2015 - 16:41
0
by Jon Moulton
Wed, 02/04/2015 - 16:41
Normal topic Pompe Disease: Block making Glycogen Synthase 1 for Substrate Reduction
by Jon Moulton » Wed, 10/29/2014 - 15:50
0
by Jon Moulton
Wed, 10/29/2014 - 15:50
Normal topic Antisense Morpholino oligo starts phase III trial
by Jon Moulton » Thu, 10/02/2014 - 16:05
0
by Jon Moulton
Thu, 10/02/2014 - 16:05
Normal topic Blocking intronic poly-A signal restores full-length expression
by Jon Moulton » Tue, 08/19/2014 - 15:13
0
by Jon Moulton
Tue, 08/19/2014 - 15:13
Normal topic Morpholinos suppress mutant huntingtin expression & attenuate neurotoxicity
by Jon Moulton » Mon, 07/07/2014 - 18:23
0
by Jon Moulton
Mon, 07/07/2014 - 18:23
Normal topic PPMO restores dystrophin, won't halt disease in late stage dko mice
by Jon Moulton » Thu, 06/19/2014 - 20:48
0
by Jon Moulton
Thu, 06/19/2014 - 20:48
Normal topic Morpholino to Intronic Repressor Element1 in SMA Mouse Models
by Jon Moulton » Tue, 04/29/2014 - 15:54
0
by Jon Moulton
Tue, 04/29/2014 - 15:54
Normal topic Dystrophin repair, mdx mice: new muscle-homing peptide-morpholino conjugate
by Jon Moulton » Wed, 04/16/2014 - 15:52
0
by Jon Moulton
Wed, 04/16/2014 - 15:52
Normal topic Antisense Oligo-Based Therapy in Human Erythropoietic Protoporphyria
by Jon Moulton » Tue, 04/01/2014 - 16:37
0
by Jon Moulton
Tue, 04/01/2014 - 16:37
Normal topic What Can We Learn From Clinical Trials of Exon Skipping for DMD?
by Jon Moulton » Thu, 03/13/2014 - 15:19
0
by Jon Moulton
Thu, 03/13/2014 - 15:19
Normal topic Parent advocacy of molecular medicine for Duchenne muscular dystrophy
by Jon Moulton » Thu, 03/06/2014 - 17:20
0
by Jon Moulton
Thu, 03/06/2014 - 17:20
Normal topic Electrophysiological Biomarkers in Spinal Muscular Atrophy: Preclinical
by Jon Moulton » Tue, 02/11/2014 - 17:10
0
by Jon Moulton
Tue, 02/11/2014 - 17:10
Normal topic Antisense suppression of donor splice site mutations in dystrophin xcript
by Jon Moulton » Thu, 02/06/2014 - 18:52
0
by Jon Moulton
Thu, 02/06/2014 - 18:52
Normal topic Make or break for first splice-modulating agents
by Jon Moulton » Mon, 11/04/2013 - 20:41
0
by Jon Moulton
Mon, 11/04/2013 - 20:41
Normal topic Context Dependent Effects of Chimeric Peptide Morpholino Conjugates
by Jon Moulton » Fri, 09/27/2013 - 17:01
0
by Jon Moulton
Fri, 09/27/2013 - 17:01
Normal topic Eteplirsen for the treatment of duchenne muscular dystrophy
by Jon Moulton » Thu, 08/01/2013 - 11:24
0
by Jon Moulton
Thu, 08/01/2013 - 11:24
Normal topic Exon skipping for SMN2: Toward a Treatment for SMA
by Jon Moulton » Fri, 04/26/2013 - 08:37
0
by Jon Moulton
Fri, 04/26/2013 - 08:37
Normal topic Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe SMA mice
by Jon Moulton » Thu, 01/24/2013 - 11:44
0
by Jon Moulton
Thu, 01/24/2013 - 11:44
Normal topic Morpholino+Peptide Neutralizes RNA Toxicity in Mouse Myotonic Dystrophy
by Jon Moulton » Mon, 01/14/2013 - 12:36
0
by Jon Moulton
Mon, 01/14/2013 - 12:36
Normal topic Dual Myostatin & Dystrophin Exon Skips by Morpholino + CPP for DMD
by Jon Moulton » Wed, 12/19/2012 - 10:45
0
by Jon Moulton
Wed, 12/19/2012 - 10:45
Normal topic Dantrolene Enhances Antisense Exon Skipping in Human & Mouse Models of DMD
by Jon Moulton » Wed, 12/12/2012 - 14:27
0
by Jon Moulton
Wed, 12/12/2012 - 14:27

Pages

New posts
No new posts
Hot topic with new posts
Hot topic without new posts
Sticky topic
Locked topic