Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe SMA mice

1 post / 0 new
Jon Moulton
Jon Moulton's picture
Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe SMA mice

Zhou H, Janghra N, Mitrpant C, Dickinson R, Anthony K, Price L, Eperon I, Wilton S, Morgan J, Muntoni F.  A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe SMA Transgenic Mice.  Hum Gene Ther. 2013 Jan 22. [Epub ahead of print]